Diagnostic and predictive methods for a Niemann-Pick disease type

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Diagnostic and predictive methods for a Niemann-Pick disease type
PDF) Genetic and laboratory diagnostic approach in Niemann Pick disease type C
Diagnostic and predictive methods for a Niemann-Pick disease type
Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment - Mengel - 2021 - Journal of Inherited
Diagnostic and predictive methods for a Niemann-Pick disease type
Niemann-Pick disease type C symptomatology: an expert-based clinical description, Orphanet Journal of Rare Diseases
Diagnostic and predictive methods for a Niemann-Pick disease type
Rare Disease Video - Niemann-Pick Disease Types A & B - National Organization for Rare Disorders
Diagnostic and predictive methods for a Niemann-Pick disease type
Niemann-Pick disease Information
Diagnostic and predictive methods for a Niemann-Pick disease type
IJMS, Free Full-Text
Diagnostic and predictive methods for a Niemann-Pick disease type
PDF) Diagnostic workup and management of patients with suspected Niemann-Pick type C disease
Diagnostic and predictive methods for a Niemann-Pick disease type
Development of a Suspicion Index to aid diagnosis of Niemann-Pick disease type C
Diagnostic and predictive methods for a Niemann-Pick disease type
At a glance: the largest Niemann-Pick type C1 cohort with 602 patients diagnosed over 15 years
de por adulto (o preço varia de acordo com o tamanho do grupo)