Niemann-Pick Type C « Niemann-Pick Children's Fund, Inc
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What is Niemann-Pick Type C Disease (NPC)? Niemann-Pick Type C Disease (NPC) simply put is FATAL. It is a genetic, neurodegenerative disorder that consequently accumulates large amounts of choleste…
Genetic disease and Niemann-Pick disorders: novel treatments and
What is Niemann-Pick Type C Disease?
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