CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
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Optic nerve regeneration screen identifies multiple genes restricting adult neural repair - ScienceDirect

OPA1 regulation of mitochondrial dynamics in skeletal and cardiac muscle - ScienceDirect

CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice
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